
SIOPEN Publications
A 2035 Clinical Research Vision and Roadmap for High-Risk Neuroblastoma
Moreno L, Dubois SG, Bird N, Knox L, Ludwinski D, Pearson ADJ, Beck-Popovic M, Bagatell R.
Development of a New Score Based on Image Defined Risk Factors to Standardize Surgical Risk in Neuroblastoma Resection - A SIOPEN Collaborative Study
Stefano Avanzini, Sabine Sarnacki, Cristian Urla, Stefano Parodi, Federico Palo, Melissa Benissad, Alessandro Crocoli, Ilaria Buconi, Paula Flores, Maria Bordallo Vazquez, Sabine Irtan, Daphne Hompes, Calogero Virgone, Martin Metzelder, Lucas Matthyssens, Hany Gabra, Nicolas Jauquier, Jorg Fuchs, Paul D. Losty, Patrizia Dall’Igna.
Recommendations for the use of nuclear medicine imaging in patients with neuroblastoma.
Sánchez-Vañó R, Balaguer J, Borrego-Dorado I, Esteban-Figueruelo A, Gámez C, Hladun R, López-Almaraz R, Llempén ML, Rodado S, Rubio-Aparicio PM.
Clin Transl Oncol. 2024 Nov 7. doi: 10.1007/s12094-024-03755-3. Epub ahead of print. PMID: 39508974.
Use Cases Requiring Privacy-Preserving Record Linkage in Paediatric Oncology
Dieter Hayn, Karl Kreiner, Emanuel Sandner, Martin Baumgartner, Bernhard Jammerbund, Markus Falgenhauer, Vanessa Düster, Priyanka Devi-Marulkar, Gudrun Schleiermacher, Ruth Ladenstein and Guenter Schreier.
Cancers 2024, 16(15), 2696; https://doi.org/10.3390/cancers16152696
Bevacizumab, Irinotecan, or Topotecan Added to Temozolomide for Children With Relapsed and Refractory Neuroblastoma: Results....
Moreno L, Weston R, Owens C, Valteau-Couanet D, Gambart M, Castel V, Zwaan CM, Nysom K, Gerber N, Castellano A, Laureys G, Ladenstein R, Rössler J, Makin G, Murphy D, Morland B, Vaidya S, Thebaud E, van Eijkelenburg N, Tweddle DA, Barone G, Tandonnet J, Corradini N, Chastagner P, Paillard C, Bautista FJ, Gallego Melcon S, De Wilde B, Marshall L, Gray J, Burchill SA, Schleiermacher G, Chesler L, Peet A, Leach MO, McHugh K, Hayes R, Jerome N, Caron H, Laidler J, Fenwick N, Holt G, Moroz V, Kearns P, Gates S, Pearson ADJ, Wheatley K; Innovative Therapies for Children with Cancer (ITCC) and European Association for Neuroblastoma Research (SIOPEN).
J Clin Oncol. 2024 Apr 1;42(10):1135-1145. doi: 10.1200/JCO.23.00458. Epub 2024 Jan 8.
Recent Evidence-Based Clinical Guide for the Use of Dinutuximab Beta in Pediatric Patients with Neuroblastoma
Balaguer J, García Hidalgo L, Hladun R, Márquez Vega C, Pérez Alonso V.
Optimising urinary catecholamine metabolite diagnostics for neuroblastoma
Yvette A H Matser, Iedan R N Verly, Maria van der Ham, Monique G M de Sain-van der Velden, Nanda M Verhoeven-Duif, Shifra Ash, Giuliana Cangemi, Sebastiano Barco, Maja Beck Popovic, André B P van Kuilenburg, Godelieve A M Tytgat ; SIOPEN Catecholamine Working Group
Pediatr Blood Cancer. 2023 Jun;70(6):e30289. doi: 10.1002/pbc.30289. Epub 2023 Apr 3
Radiotherapy quality assurance in paediatric clinical trials: first report from six QUARTET-affiliated trials
Sarah M Kelly, Andrada Turcas, Coreen Corning, Simon Bailey, Adela Cañete, Enrico Clementel, Andrea di Cataldo, Karin Dieckmann, Mark N Gaze, Gail Horan, Meriel Jenney, Ruth Ladenstein, Laetitia Padovani, Dominique Valteau-Couane, Tom Boterberg, Henry Mandeville
Radiother Oncol. 2023 May;182:109549. doi: 10.1016/j.radonc.2023.109549. Epub 2023 Feb 23
Overcoming inter-observer planning variability in target volume contouring and dose planning …
for high-risk neuroblastoma - a European multicenter effort of the SIOPEN radiotherapy committee
Danny Jazmati, Lorenzo Brualla, Annemieke S Littooij, Britta Webber, Karin Dieckmann, Geert O Janssens, Thorsten Simon, Mark N Gaze , Julien Merta, Antonio Serrano, Stefan Dietzsch, Paul-Heinz Kramer, Jörg Wulff, Tom Boterberg, Beate Timmermann
Radiother Oncol. 2023 Apr;181:109464. doi: 10.1016/j.radonc.2023.109464. Epub 2023 Jan 11
Early-phase clinical trial eligibility and response evaluation criteria for refractory, relapsed, or progressive neuroblastoma: …
…A consensus statement from the National Cancer Institute Clinical Trials Planning Meeting.
Park JR, Villablanca JG, Hero B, Kushner BH, Wheatley K, Beiske KH, Ladenstein RL, Baruchel S, Macy ME, Moreno L, Seibel NL, Pearson AD, Matthay KK, Valteau-Couanet D.
Cancer. 2022 Nov 1;128(21):3775-3783. doi: 10.1002/cncr.34445. Epub 2022 Sep 13. PMID: 36101004
Presenting features of neuroblastoma with spinal canal invasion. A prospective study of … (SIOPEN)
Sorrentino S, Ash S, Haupt R, Plantaz D, Schiff I, Hero B, Simon T, Kachanov D, Shamanskaya T, Kraal K, Littooij A, Wieczoreck A, Balwierz W, Laureys G, Trager C, Sertorio F, Erminio G, Fragola M, Beck Popovic M, De Bernardi B, Trahair T.
Suprarenal Masses in Very Young Infants: Is It Safe to Watch and Wait? Report of a SIOPEN Observational Study Results.
Papadakis V, Segura V, Conte M, Plantaz D, Di Cataldo A, Schleiermacher G, Wheeler K, Bermúdez JD, Ash S, Brichard B, Ladenstein R, Combaret V, Sarnacki S, Fagnani AM, Granata C, Cañete A.
Clinical Phenotype and Management of Severe Neurotoxicity Observed in Patients with Neuroblastoma Treated with Dinutuximab Beta in Clinical Trials
Wieczorek A., Manzitti C., Garaventa A., Gray J., Papadakis V., Valteau-Couanet D., Zachwieja K., Poetschger U., Pribill I., Fiedler S., Ladenstein R., Lode HN
Cancers (Basel) 2022, 14(8), 1919; https://doi.org/10.3390/cancers14081919, 2022 April 10 (link 2)
A Phase II Trial of a Personalized, Dose-Intense Administration Schedule of 177Lutetium-DOTATATE in Children…
…With Primary Refractory or Relapsed High-Risk Neuroblastoma-LuDO-N
Fredrik Sundquist Kleopatra Georgantzi, Kirsten Brunsvig Jarvis, Jesper Brok, Minna Koskenvuo, Jelena Rascon, Max van Noesel, Per Grybäck, Joachim Nilsson, Arthur Braat, Mikael Sundin, Sandra Wessman, Nikolas Herold, Lars Hjorth, Per Kogner, Dan Granberg, Mark Gaze, Jakob Stenman
Front Pediatr 2022 Mar 10;10:836230. doi: 10.3389/fped.2022.836230. eCollection 2022.
A Novel Standard for Systematic Reporting of Neuroblastoma Surgery: The International Neuroblastoma Surgical Report Form (INSRF): ...
A Joint Initiative by the Pediatric Oncological Cooperative Groups SIOPEN, COG, and GPOH
Lucas E Matthyssens, Jed G Nuchtern, Cees P Van De Ven, Hany O S Gabra, Kristin Bjornland, Sabine Irtan, Jakob Stenman, Luca Pio, Kate M Cross, Stefano Avanzini, Alessandro Inserra, Javier Gomez Chacon, Patrizia Dall'igna, Dietrich Von Schweinitz, Keith Holmes, Jorg Fuchs, Roly Squire, Dominique Valteau-Couanet, Julie R Park, Angelika Eggert, Paul D Losty, Michael P La Quaglia, Sabine Sarnacki, Surgical and Medical Committees of SIOPEN, COG and GPOH
Ann Surg. 2022 Mar 1;275(3):e575-e585. doi: 10.1097/SLA.0000000000003947.
Minimally invasive surgery for neuroblastic tumours: A SIOPEN multicentre study: Proposal for guidelines.
Gabra HO, Irtan S, Cross K, Lobos P, Froeba-Pohl A, Pio L, Virgone C, Guillén Burrieza G, Gómez Chacón Villalba J, Riccipetitoni G, Guérin F, Nightingale M, Heloury Y, Faraj S, Leclair M, Scalabre A, Mattioli G, Warmann SW, Fuchs J, Basta N, Bjørnland K, Matthyssens LE, Losty PD, Sarnacki S.
Frequency and Prognostic Impact of ALK Amplifications and Mutations in the SIOPEN HR-NBL-1 trial
Angela Bellini, Ulrike Pötschger, Virginie Bernard, Eve Lapouble, Sylvain Baulande, Peter F Ambros, Nathalie Auger, Klaus Beiske, Marie Bernkopf, David R Betts, Jaydutt Bhalshankar, Nick Bown, Katleen de Preter, Nathalie Clément, Valérie Combaret, Jaime Font de Mora, Sally L George, Irene Jiménez, Marta Jeison, Barbara Marques, Tommy Martinsson, Katia Mazzocco, Martina Morini, Annick Mühlethaler-Mottet, Rosa Noguera, Gaelle Pierron, Maria Rossing, Sabine Taschner-Mandl, Nadine Van Roy, Ales Vicha, Louis Chesler, Walentyna Balwierz, Victoria Castel, Martin Elliott, Per Kogner, Geneviève Laureys, Roberto Luksch, Josef Malis, Maja Popovic-Beck, Shifra Ash, Olivier Delattre, Dominique Valteau-Couanet, Deborah A Tweddle, Ruth Ladenstein, Gudrun Schleiermacher
J Clin Oncol . 2021 Oct 20;39(30):3377-3390. doi: 10.1200/JCO.21.00086. Epub 2021 Jun 11.
Randomised trial of two induction therapy regimens for high-risk neuroblastoma HR-NBL1.5 …
International Society of Paediatric Oncology European Neuroblastoma Group Study
Alberto Garaventa, Ulrike Pötschger, Dominique Valteau-Couanet, Roberto Luksch, Victoria Castel, Martin Elliott, Shifra Ash, Godfrey CF Chan, Geneviève Laureys, Maja Beck-Popovic, Kim Vettenranta, Walentyna Balwierz, Henrik Schröder, Cormac Owens, Cesen Maja, Vassilios Papadakis, Toby Trahair, Gudrun Schleiermacher, Peter Ambros, Stefania Sorrentino, Andrew DJ Pearson, Ruth Ladenstein,
J Clin Oncol . 2021 Aug 10;39(23):2552-2563. doi: 10.1200/JCO.20.03144. Epub 2021 Jun 21.
Central nervous system relapse in high-risk stage 4 neuroblastoma: The HR-NBL1/SIOPEN trial experience
P Berlanga, C Pasqualini, U Pötschger, C Sangüesa, M R Castellani, A Cañete, R Luksch, M Elliot, G Schreier, M Kropf, D Morgenstern, V Papadakis, S Ash, E Ruud, P Brock, A Wieczorek, P Kogner, T Trahair, P Ambros, T Boterberg, V Castel, D Valteau-Couanet, R Ladenstein
Eur J Cancer. 2021 Feb;144:1-8. doi: 10.1016/j.ejca.2020.10.020. Epub 2020 Dec 11.
Age Dependency of the Prognostic Impact of Tumor Genomics in Localized Resectable MYCN-Nonamplified Neuroblastomas.
Report From the SIOPEN Biology Group on the LNESG Trials and a COG Validation Group
Ambros IM, Tonini GP, Pötschger U, Gross N, Mosseri V, Beiske K, Berbegall AP, Bénard J, Bown N, Caron H, Combaret V, Couturier J, Defferrari R, Delattre O, Jeison M, Kogner P, Lunec J, Marques B, Martinsson T, Mazzocco K, Noguera R, Schleiermacher G, Valent A, Van Roy N, Villamon E, Janousek D, Pribill I, Glogova E, Attiyeh EF, Hogarty MD, Monclair TF, Holmes K, Valteau-Couanet D, Castel V, Tweddle DA, Park JR, Cohn S, Ladenstein R, Beck-Popovic M, De Bernardi B, Michon J, Pearson ADJ, Ambros PF.
J Clin Oncol. 2020 Sep 9:JCO1802132. doi: 10.1200/JCO.18.02132. Epub ahead of print. PMID: 32903140.